Search for Clinical Trial Results

Dysferlinopathy - 4 Studies Found
Status | Study |
Recruiting |
Study Name: rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies Condition: Dysferlinopathy Date: 2016-02-11 Interventions: Drug: rAAVrh74.MHCK7.DYSF.DV Biological/Vaccine: rAAVrh74.MHCK7.DYSF.DV Recombinant adeno-associated vir |
Completed |
Study Name: Deflazacort in Dysferlinopathies Condition:
|
Active, not recruiting |
Study Name: Clinical Outcome Study for Dysferlinopathy Condition:
|
Recruiting |
Study Name: Proteasomal Inhibition for Patients With Mis-sense Mutated Dysferlin Condition: Dysferlinopathy Date: 2013-04-29 Interventions: Drug: Bortezomib Other Name: Velcade® |