Search for Clinical Trial Results

GM1 Gangliosidosis - 8 Studies Found
Status | Study |
Recruiting |
Study Name: Synergistic Enteral Regimen for Treatment of the Gangliosidoses Condition:
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Recruiting |
Study Name: A Natural History Study of the Gangliosidoses Condition:
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Completed |
Study Name: HSCT for High Risk Inherited Inborn Errors Condition:
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Recruiting |
Study Name: Biomarker for GM1/GM2 - Gangliosidoses Condition:
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Recruiting |
Study Name: Nervous System Degeneration in Glycosphingolipid Storage Disorders Condition:
Date: 2002-01-27 |
Completed |
Study Name: Reduced-Intensity Hematopoietic Stem Cell Transplant for High Risk Lysosomal and Peroxisomal Disorders Condition:
Date: 2012-06-20 Interventions:
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Terminated |
Study Name: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases Condition:
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