Search for Clinical Trial Results

Sponsored By

Leigh Syndrome - 10 Studies Found

Status Study
Completed Study Name: Safety and Efficacy Study of EPI-743 in Children With Leigh Syndrome
Condition: Leigh Syndrome
Date: 2012-11-01
Interventions:
  • Drug: Placebo
  • Drug: EPI-743 15 mg/kg
Enrolling by invitation Study Name: Long-Term Safety and Efficacy Evaluation of EPI-743 in Children With Leigh Syndrome
Condition: Leigh Syndrome
Date: 2014-08-21
Interventions: Drug: EPI-743 EPI-743 is a quinone oxidation product of alpha tocotrienol
Recruiting Study Name: The Leigh Syndrome Registry
Condition:
  • Leigh Syndrome
  • Leigh Disease

    • Date: 2017-04-28
Completed Study Name: Open-Label, Dose-Escalating Study Assessing Safety, Tolerability, Efficacy, of RP103 in Mitochondrial Disease
Condition: Inherited Mitochondrial Disease, Including Leigh Syndrome
Date: 2013-12-17
Interventions: Drug: Cysteamine Bitartrate Cysteamine Bitartrate Delayed-release Capsules
Completed Study Name: A Dose-escalating Clinical Trial With KH176
Condition:
  • MELAS
  • LHON
  • Leigh Syndrome Date: 2015-04-19
    Interventions:
    • Drug: KH176
    • Drug: placebo
Enrolling by invitation Study Name: Tissue Sample Study for Mitochondrial Disorders
Condition:
  • Mitochondrial Disorders
  • Mitochondrial Disease
  • Melas
    • <
    Date: 2012-08-31
Recruiting Study Name: Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
Condition:
  • Rare Disorders
  • Undiagnosed Disorders
  • Disorders of Unknown
    Date: 2013-02-13
Active, not recruiting Study Name: EPI-743 for Mitochondrial Respiratory Chain Diseases
Condition: Mitochondrial Diseases
Date: 2011-06-07
Interventions: Drug: EPI-743 EPI-743 is administered as a dose escalation from 50 mg bid to 100 mg tid
Completed Study Name: A Long-Term Extension Study of RP103-MITO-001 (NCT02023866) to Assess RP103 in Children With Inherited Mitochondrial Disease
Condition: Mitochondrial Diseases
Date: 2015-06-10
Interventions: Drug: Cysteamine Bitartrate Delayed-release Capsules Treatment with experimental drug as detailed in arm
Recruiting Study Name: North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
Condition:
  • Mitochondrial Disorders
  • Mitochondrial Genetic Disorders
  • Mi
    Date: 2012-09-25